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Antisense suppression of donor splice site mutations for DMD

Jon Moulton
Gene Tools, LLC
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Antisense suppression of donor splice site mutations for DMD
Thu, Feb 06, 2014, 12:55 pm CST

Fletcher S, Meloni PL, Johnsen RD, Wong BL, Muntoni F, Wilton SD.  Antisense suppression of donor splice site mutations in the dystrophin gene transcript.  Mol Genet Genomic Med. 2013 Sep;1(3):162-73. doi: 10.1002/mgg3.19. Epub 2013 Jun 13.

Antisense suppression of donor splice site mutations for DMD
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