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What Can We Learn From Clinical Trials of Exon Skipping for DMD?

Jon Moulton
Gene Tools, LLC
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What Can We Learn From Clinical Trials of Exon Skipping for DMD?
Thu, Mar 13, 2014, 10:21 am CDT

What Can We Learn From Clinical Trials of Exon Skipping for DMD?

Qi-long Lu, Sebahattin Cirak and Terence Partridge.

Citation: Molecular Therapy Nucleic Acids. 2014;3,e152; doi:10.1038/mtna.2014.6

http://www.nature.com/mtna/journal/v3/n3/full/mtna20146a.html

What Can We Learn From Clinical Trials of Exon Skipping for DMD?
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