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Exon skipping and splice modulation therapies for neuromuscular diseases

Jon Moulton
Gene Tools, LLC
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Exon skipping and splice modulation therapies for neuromuscular diseases
Fri, Mar 14, 2014, 3:24 pm CDT

Touznik A, Lee JJ, Yokota T. New developments in exon skipping and splice modulation therapies for neuromuscular diseases. Expert Opin Biol Ther. 2014 Mar 12. [Epub ahead of print]

Exon skipping and splice modulation therapies for neuromuscular diseases
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