This is another step toward using Morpholino oligos as therapeutics for Duchenne muscular dystrophy.
Doran P, Wilton SD, Fletcher S, Ohlendieck K. Proteomic profiling of antisense-induced exon skipping reveals reversal of pathobiochemical abnormalities in dystrophic mdx diaphragm. Proteomics. 2009 Jan 8. [Epub ahead of print]
http://www.ncbi.nlm.nih.gov/pubmed/19132684
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